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Aromatic L-Amino Acid Decarboxylase

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Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Trial in Shanghai (VGN-R09b)

Recruiting
  • Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
  • Shanghai, No. 1678, Dongfang Road, Pudong New Area, Shanghai, China
    Shanghai Children's Medical Center Affiliated to Shanghai Jiao T
Mar 9, 2023

Aromatic L-Amino Acid Decarboxylase Deficiency Trial in Angers, Toulouse (Plasmatic 3-O-Methyldopa dosage)

Recruiting
  • Aromatic L-Amino Acid Decarboxylase Deficiency
  • Plasmatic 3-O-Methyldopa dosage
  • Angers, France
  • +1 more
Aug 10, 2022

AADC/TDC in Advanced Parkinson's Disease

Not yet recruiting
  • Parkinson Disease
    • (no location specified)
    Dec 9, 2022

    Aromatic Amino Acid Decarboxylase Deficiency Trial in Taipei (AAV2-hAADC)

    Active, not recruiting
    • Aromatic Amino Acid Decarboxylase Deficiency
    • Taipei, Taiwan
      National Taiwan University Hospital
    Nov 15, 2021

    Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Trial in Taipei (gene therapy)

    Active, not recruiting
    • Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
    • gene therapy
    • Taipei, Taiwan
      National Taiwan University Hospital
    Aug 4, 2021

    AADC Deficiency Trial in San Francisco, Columbus (AAV2-hAADC)

    Recruiting
    • AADC Deficiency
    • San Francisco, California
    • +2 more
    Jan 14, 2022

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Type I Diabetes Trial in Birmingham (Placebo GABA and Placebo GAD-alum, GABA and Placebo GAD-alum, Active Oral GABA and Active

      Completed
      • Type I Diabetes
      • Placebo GABA and Placebo GAD-alum
      • +2 more
      • Birmingham, Alabama
        Children's of Alabama
      May 2, 2022

      Phenylketonurias Trial in Birmingham (Casein, L-amino acids, CGMP-AA)

      Active, not recruiting
      • Phenylketonurias
      • Casein
      • +2 more
      • Birmingham, West Midlands, United Kingdom
        University Hospitals Birmingham NHS Foundation Trust
      Jul 25, 2023

      Parkinson Disease Trial in Shimotsuke (Cohort1, Cohort2)

      Terminated
      • Parkinson Disease
      • Cohort1
      • Cohort2
      • Shimotsuke, Tochigi, Japan
        Jichi Medical University
      Aug 7, 2019

      Parkinson's Disease Trial in United States (VY-AADC02, Sham (Placebo) Surgery)

      Active, not recruiting
      • Parkinson's Disease
      • VY-AADC02
      • Sham (Placebo) Surgery
      • Irvine, California
      • +19 more
      Mar 17, 2022

      Long-term Extension Study for Participants of Prior VY-AADC01

      Enrolling by invitation
      • Parkinson's Disease
        • San Francisco, California
          University of California, San Francisco
        Mar 17, 2022

        Pregnancy Related Trial in Vancouver (Aromatic Amino Acid Intake)

        Completed
        • Pregnancy Related
        • Aromatic Amino Acid Intake
        • Vancouver, British Columbia, Canada
          Clinical Research and Evaluation Unit
        Sep 22, 2020

        Vitamin D Deficiency Trial in Shreveport (Vitamin D, Placebo, Vitamin D + L-cysteine)

        Recruiting
        • Vitamin D Deficiency
        • Vitamin D
        • +3 more
        • Shreveport, Louisiana
          Louisiana State University Health Shreveport
        Sep 2, 2022

        Phenylketonurias Trial in Kobenhavn, Bristol, Birmingham (CGMP protein substitute, L-amino acid protein substitute)

        Active, not recruiting
        • Phenylketonurias
        • CGMP protein substitute
        • L-amino acid protein substitute
        • Kobenhavn, Denmark
        • +2 more
        Sep 15, 2022

        Diabetes, Diabetic Peripheral Neuropathy, Diabetic Foot Ulcer Trial in Columbia (Lovaza, L-Arginine Powder, Vitamin C)

        Enrolling by invitation
        • Diabetes Mellitus
        • +2 more
        • Columbia, South Carolina
          Prisma Health
        Jan 10, 2023

        Cerebral Palsy, Genetic Disease, Developmental Delay Trial in Ljubljana (NGS)

        Completed
        • Cerebral Palsy
        • +3 more
        • NGS
        • Ljubljana, Slovenia
          University Children's Hospital, University Medical Centre Ljublj
        Nov 1, 2022

        Localized Osteosarcoma, Metastatic Osteosarcoma, Resectable Osteosarcoma Trial (Bone Scan, Cabozantinib S-malate, Cisplatin)

        Not yet recruiting
        • Localized Osteosarcoma
        • +3 more
        • Cabozantinib S-malate
        • +7 more
        • (no location specified)
        Jan 4, 2023

        Idiopathic Parkinson's Disease, Parkinson's Disease, Basal Ganglia Disease Trial in United States (VY-AADC01)

        Completed
        • Idiopathic Parkinson's Disease
        • +8 more
        • San Francisco, California
        • +3 more
        Mar 17, 2022

        Neurosciences Trial (Précurseur de la dopamine, antagoniste D2, PLACEBO)

        Not yet recruiting
        • Neurosciences
        • Précurseur de la dopamine
        • +2 more
        • (no location specified)
        Feb 1, 2023

        B Acute Lymphoblastic Leukemia Trial (procedure, biological, drug, radiation)

        Not yet recruiting
        • B Acute Lymphoblastic Leukemia
        • Biospecimen Collection
        • +19 more
        • (no location specified)
        Nov 8, 2023

        AADC Deficiency Trial in Israel, Taiwan, United States (Eladocagene Exuparvovec)

        Recruiting
        • AADC Deficiency
        • Eladocagene Exuparvovec
        • Palo Alto, California
        • +6 more
        Aug 4, 2022

        Non Small Cell Lung Cancer, NSCLC, Stage III, Nsclc Trial in Stanford (Durvalumab, Carboplatin, Pemetrexed)

        Recruiting
        • Non Small Cell Lung Cancer
        • +2 more
        • Stanford, California
          Stanford University
        Oct 27, 2022

        Amino Acid, Body Weight Changes, Skin Manifestations Trial in Pavia (L-glutamine, L-arginine and calcium

        Completed
        • Amino Acid
        • +4 more
        • L-glutamine, L-arginine and calcium beta-hydroxy-beta-methylbutyrate
        • Placebo
        • Pavia, Italy
          Azienda di Servizi alla Persona
        Jan 7, 2021

        Parkinson Disease Trial in Lille (A-dopamine, optimized oral treatment)

        Recruiting
        • Parkinson Disease
        • Lille, France
          Hopital Roger Salengro, CHU Lille
        Oct 11, 2022